Pushing through her tears and fears, columnist Connie Chandler realizes that vulnerability is not the opposite of strength.

Pain medication was supposed to improve columnist Sherry Toh's functionality, but even after a year, the side effects can ...

A real-world study in Spain found adults and children with SMA show high long-term adherence to daily treatment with oral ...

Using disease-modifying therapies may help children with SMA types 1 and 2 maintain better nutrition and prevent stunted ...

Spinraza was linked to changes in CSF biomarkers in SMA, some of which were associated with motor gains, but more research is ...

Columnist Connie Chandler shares how a simple childhood craft allowed her to be genuinely seen by others and form ...

Spinraza was shown to slow lung function decline for symptomatic spinal muscular atrophy patients, but ventilation was still ...

Evidence-based guidelines have been developed for newborn screening, diagnosis, and early management of SMA in Australia and ...

Columnist Sherry Toh pushes back against narratives that blame parents for a child's disability, and instead thanks her ...

As columnist Helen Baldwin prepares to celebrate the 29th birthday of her son, who died from SMA in 1997, she welcomes a new ...

In episode 158, host Kevin Schaefer talks with Alberto Lopez from Los Angeles County, California. Alberto is a consultant and… ...

Haloperidol, an antipsychotic, shows promise for SMA treatment. It increases SMN protein, protects motor neurons, and improves motor function in models. Further clinical evaluation is needed to ...