Pain medication was supposed to improve columnist Sherry Toh's functionality, but even after a year, the side effects can ...

Spinraza was shown to slow lung function decline for symptomatic spinal muscular atrophy patients, but ventilation was still ...

A real-world study in Spain found adults and children with SMA show high long-term adherence to daily treatment with oral ...

Columnist Connie Chandler shares how a simple childhood craft allowed her to be genuinely seen by others and form ...

Using disease-modifying therapies may help children with SMA types 1 and 2 maintain better nutrition and prevent stunted ...

Spinraza was linked to changes in CSF biomarkers in SMA, some of which were associated with motor gains, but more research is ...

Evidence-based guidelines have been developed for newborn screening, diagnosis, and early management of SMA in Australia and ...

SMA newborn screening may help children start treatment earlier, supporting better independence and daily function at school ...

Caregiving can involve multitasking, but columnist Connie Chandler asks what do you do when your caregiver is better at one ...

Columnist Sherry Toh pushes back against narratives that blame parents for a child's disability, and instead thanks her ...

As columnist Helen Baldwin prepares to celebrate the 29th birthday of her son, who died from SMA in 1997, she welcomes a new ...

Haloperidol, an antipsychotic, shows promise for SMA treatment. It increases SMN protein, protects motor neurons, and improves motor function in models. Further clinical evaluation is needed to ...